Patients & Caregivers
We're Here to Help
We provide resources and support to patients and their families throughout their journey
Through collaboration, compassion, and partnership, we provide support that empowers. We also work with advocacy groups around the world to help raise awareness of the unique challenges our community faces.
A personal guide for navigating treatment
With our PTC Cares™ program, you can receive personalized support to gain access to treatment. Our case managers are here to help address any potential challenges.
Clinical Trials at PTC
PTC is conducting clinical trials in a variety of disease areas. New ones are continually being added.