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About PTC

Patients are our priority

Over the last 25 years, everything we’ve done, every study, every experiment, every investment is made first and foremost to change the course of rare diseases for the lives of our patients.

A history of innovation

For over two decades, we have achieved historic breakthroughs in the treatment of rare diseases. We have been a pioneer in the development of treatments for rare diseases and we will continue to generate life-changing treatments around the globe for the next 25 years and beyond.

View our history

A deeper look at PTC

Our team
Brilliant minds and passion for patients come together here
Meet the Leadership Team
Global impact
Caring for our environment, our people, and our community have been part of PTC’s fabric since its founding
Responsibility at PTC

Be extraordinary with us

PTC is looking for people with determination and kindness to provide life-changing treatments. Join us on our mission to help people with rare diseases. They are counting on us.

Matt Klein and Mary Frances Harmon

Gene Therapy Manufacturing

We established a Gene Therapy Center of Excellence to provide access to treatments for our patients and partners.

Gene Therapy Technical Center of Excellence

We'd love to hear from you