Patients are our priority
measured by moments
PTC is committed to providing access to best-in-class treatments for patients with little to no treatment options.
This mission underpins our focus on the discovery, development, and global commercialization of clinically differentiated medicines for those with rare diseases.
As a science-driven, global pharmaceutical company, we combine clinical and scientific expertise with groundbreaking science and technology. We work hard to provide broad access to our life-changing treatments. What drives us is our passion to provide patients with more moments with their families.
For over two decades, we have achieved historic breakthroughs in the treatment of rare diseases. We have been a pioneer in the development of treatments for rare diseases and we will continue to generate life-changing treatments around the globe for the next 25 years and beyond.
A deeper look at PTC
