Therapeutic areas
Diseases we’re on a mission to change
Since its inception, PTC has been viewed as an expert in RNA biology. Today, our biotechnology platforms have expanded, but harnessing the most promising scientific approach to target the root cause of a disorder has remained constant.
Metabolism
Neurology
Oncology
Clinical Trials at PTC
Developing an array of potential therapies
PTC is conducting a wide range of clinical trials in a variety of rare diseases. Interested in enrolling in a clinical trial?