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Education for Duchenne Caregivers in Hungary

August 28, 2020

  1. Education for Duchenne Caregivers in Hungary

    “For many parents of Duchenne patients in Hungary, these events provide a trusted environment where they can share their concerns, and experience a few well-needed hours of respite as their child takes part in many fun activities with their peers.” – Dr Gabriella Oberrecht, Chairperson of the Board, Healing Goodwill Foundation – Duchenne Hungary Receiving…

  2. Counseling Duchenne Patients in Russia

    “With so many individuals providing care to their child alone, without professional help, the ‘Not Alone’ initiative, made possible by the STRIVE program, will provide an invaluable support system to families impacted by Duchenne muscular dystrophy.” – Margarita Urmancheeva, President, GAOORDI Due to a lack of funding, only a few specialist care facilities for Duchenne…

  3. PTC Grant Funds Life Science Immersion Program

    “The next young generation can play a pivotal role in supporting the rare disease community. With this year’s STRIVE Award, we can equip students with the essential tools and knowledge needed so they can be young Duchenne ambassadors in their community.” – Richard Horgan, Founder and President, Cure Rare Disease The rarity of diseases such…

  4. Advancing Gene Therapies – Interview with Mark Pykett, CSO

    Gene therapy can revolutionize how we treat patients with rare diseases. As we work to discover and develop therapeutics for patients living with genetic disorders, PTC Chief Scientific Officer, Mark Pykett, explains our strategy and goals for gene therapy. “PTC is a global company with a commitment spanning more than two decades to patients with…

  5. PTC Awards Grants for Global Duchenne Muscular Dystrophy Research

    In 2019, we launched PRIORITY, a global innovative research funding program to support pioneering clinical research initiatives that address the unmet medical needs of patients with the rare genetic disorder Duchenne muscular dystrophy. The goal is to advance the diagnosis and care of patients and support unique research programs that are focused on increasing the number…