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PTC applies its expertise in RNA biology and drug development to pioneer novel oral treatments for patients living with serious and life-threatening conditions.
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:: About Us
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Leadership
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Working at PTC
:: Our Approach
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Post-Transcriptional Control
RNA Biology
GEMS
:: Therapeutic Areas
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Genetic Disorders
Ataluren
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Oncology
PTC299
Infectious Diseases
Drug Discovery Programs
:: Clinical Trials
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Ataluren
PTC299
:: News & Resources
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GEMS
Overview
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Overview
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