Clinical trials provide the medical community with valuable research and data that helps to facilitate the development of new and potentially life-saving therapies. By participating in a clinical trial, you are taking an active role in the development and approval of new medicines and treatments.

There is a lot to learn about clinical trials – from what they are and how they work, to questions to consider, to the participant journey. Insightful Moments™ is here to help!

Insightful Moments is a community education series of programs and materials created to support patients with rare disease and their families. Read on to learn more about every step of the journey with our Navigating Clinical Trials resources:

First, what are clinical trials?

Now that you know about clinical trials, check out this roadmap to learn how to find one that might be right for you.

There are a lot of things to think about when considering participating in a clinical trial. Check out this helpful roadmap from Insightful Moments on all the questions to consider.

If you are already on your way to participating in a clinical trial, check out this roadmap to learn about the participant journey.

And finally, read this fact sheet to learn more about informed consent, which is the process of telling potential research participants about the key elements of a research study and what their participation will involve.

All of this information can also be found on our Insightful Moments page.

If you have questions or want to learn more, please call 1-833-PTC-HOPE (1-833-782-4673) or email us at