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2022: A Year of Many Firsts

December 15, 2022

  1. 2022: A Year of Many Firsts

    For PTC, 2022 was a milestone-reaching, patient-supporting, award-winning, employee-engaging, community-driven year. It was also another year of many firsts. The first approved disease-modifying treatment for AADC deficiency, and the first marketed gene therapy directly infused into the brain, was approved in Europe and the UK. We also had the first global regulatory approval for treatment…

  2. Meet the Swiss National Team for the 2022 IWAS Wheelchair Hockey World Cup

    Powerchair hockey is a team sport played by athletes who require the use of an electric wheelchair in their day-to-day lives. Athletes have disabilities ranging from Muscular Dystrophy or SMA, to cerebral palsy or severe spinal cord injuries. Learn More about the 2022 IWAS Powerchair Hockey World Cup Meet the Swiss National Team

  3. “On the playing field I am an athlete instead of a wheelchair user”

    ”Your child is severely physically disabled” – after giving this kind of diagnosis, physicians are faced with an important task: to give desperate parents some perspective. Impossible? Not at all! Because even with a severe disability, so much is possible – sometimes even a world championship title. Let yourself be inspired. Sport at the highest…

  4. IWAS Powerchair Hockey Game Schedule

    Powerchair hockey is a team sport played by athletes who require the use of an electric wheelchair in their day-to-day lives. Athletes have disabilities ranging from Muscular Dystrophy or SMA, to cerebral palsy or severe spinal cord injuries. Learn More about the 2022 IWAS Powerchair Hockey World Cup

  5. Supporting the 2022 IWAS Powerchair Hockey World Cup!

    At PTC Therapeutics, we continue to be inspired by the communities we serve. We are proud to be sponsoring this year’s IWAS Powerchair Hockey World Cup, which is taking place from the 9th – 14th August 2022, in Switzerland. The IWAS Powerchair Hockey World Cup is the most important international competition for powerchair hockey athletes.…

  6. Introducing Insightful Moments™, a Rare Disease Patient Education Series

    En español haz clic aquí Living with a rare disease or caring for someone with a rare disease comes with many challenges. In addition to processing new and complicated information and making countless decisions, it can be tough to know where to turn to for help, or where to even begin. To help support patients…

  7. Our Commitment to the Rare Disease Community

    PTC was founded in 1998 by a scientist with a desire to serve patients with rare diseases and unmet medical needs. Over the course of our history, we have grown to a team of more than a thousand employees and developed new innovative therapies. However, we’ve always maintained our foundational commitment to our patients and…

  8. SMA Therapy: A Winding Path to Success

    Learn how PTC Therapeutics developed our spinal muscular atrophy (SMA) therapy from our founder and CEO Stuart Peltz, VP & Head of Group External Affairs and Alliance Management Nikolai Naryshkin, and other members of our dedicated team.