A few important resources for patients and families.
- Action Duchenne - www.actionduchenne.org
- Cystic Fibrosis Foundation (CFF) - www.cff.org
- Cystic Fibrosis Research, Inc. - www.cfri.org
- FDA Clinical Trials Website - www.clinicaltrials.gov
- Gene Tests: NIH-Sponsored Website - www.genetests.org
- Muscular Dystrophy Association - www.mdausa.org
- National Organization for Rare Disorders (NORD) - www.rarediseases.org
- Parent Project Muscular Dystrophy (PPMD) - www.parentprojectmd.org
- TREAT-NMD Neuromuscular Network (Translational Research in Europe for the Assessment and Treatment of Neuromuscular Disease) - www.treat-nmd.eu
Please note that external web site links provided on this webpage are outside of PTC Therapeutics' control, and we assume no responsibility for the information they may contain. These external links are provided for educational purposes only and are not intended to replace the medical advice of a physician or other qualified health care provider.