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The ataluren (PTC124™) Phase 2b trial in nonsense mutation Duchenne and Becker muscular dystrophy involves 37 sites on four continents, as shown on the map below. As you click on each region, you will be able to see names and locations of specific sites. The trial is a multi-center, randomized, double-blind, placebo-controlled study to determine whether ataluren can improve walking, activity, muscle function, and strength and whether the drug can safely be given for a long period of time.
Australia |
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Royal Children's Hospital
Parkville, Victoria
Principal Investigator: Monique Ryan, M.D.
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Institute For Neuromuscular
Research, The Children's Hospital at Westmead
Westmead, NSW
Principal Investigator: Kristi Jones, M.D.
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Belgium |
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University Hospital KU Leuven
Leuvan, Belgium
Principal Investigator: Nathalie Goemans, M.D.
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Canada |
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Alberta Children's Hospital
Calgary, Alberta
Principal Investigator: Jean Mah, M.D.
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London Health Sciences Center
London, Ontario
Principal Investigator: Craig Campbell, M.D.
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British Columbia Children's Hospital
Vancouver, British Columbia
Principal Investigator: Katherine Selby, M.D.
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France |
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Service de Neuropediatrie, hôpital La Timone
Marseille, France
Principal Investigator: Brigitte Chabrol, M.D.
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Neuromuscular center of Nantes
Nantes, France
Principal Investigator: Yann Pereon, M.D.
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Groupe Hospitalier La Pitie-Salpetriere
Paris, France
Principal Investigator: Thomas Voit, M.D.
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Germany |
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University Clinic for Children, University of Essen
Essen, Germany
Principal Investigator: Ulrike Schara, M.D. |
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University Hospital
Freiburg, Germany
Principal Investigator: Jan Kirschner, M.D.
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Israel |
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Hadassah Medical Center, Hebrew University Hospital
Jerusalem, Israel
Principal Investigator: Yoram Nevo, M.D. |
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Italy |
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Ospedale Maggiore Policlinico in Milan
Milan, Italy
Principal Investigator: Pr. Giacomo Comi, M.D. |
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Ospedale Pediatrico Bambino Gesu
Rome, Italy
Principal Investigator: Enrico Bertini, M.D.
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U.O. Complessa di Neuropsichiatria Infantile
Rome, Italy
Principal Investigator: Eugenio Mercuri, M.D.
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Spain |
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Hospital Sant Joan de déu
Barcelona, Spain
Principal Investigator: Jaume Colomer, M.D.
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Hospital Universitari La Fe
Valencia, Spain |
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Sweden |
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Queen Silvia Children's Hospital
Goteburg, Sweden
Principal Investigator: Mar Tulinius, M.D.
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Astrid Lindgren Pediatric Hospital
Stockholm, Sweden
Principal Investigator: Thomas Sejersen, M.D.
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United Kingdom |
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Imperial College London, Hammersmith Hospital
London, UK
Principal Investigator: Francesco Muntoni, M.D.
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Univ of Newcastle, Institute of Human Genetics
Newcastle, UK
Principal Investigator: Katharine Bushby, M.D.
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Robert Jones and Agnes Hunt Orthopaedic NHS Trust
Shropshire, UK
Principal Investigator:Ros Quinlivan, M.D.
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USA |
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University of California-Davis
Sacramento, CA
Principal Investigator: Craig McDonald, M.D.
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The Children's Hospital
Aurora, CO
Principal Investigator: Susan Apkon, M.D.
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Child Neurology Center of Pensacola
Pensacola, FL
Principal Investigator: Ben Renfroe, M.D.
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University of Iowa Healthcare
Iowa City, IA
Principal Investigator: Kathy Mathews, M.D.
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University of Kansas Medical Centre
Kansas City, KS
Principal Investigator:Richard Barohn, M.D. |
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Children's Hospital of Boston/Harvard Medical School
Boston, MA
Principal Investigator: Basil Darras, M.D.
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University of Minnesota
Minneapolis, MN
Principal Investigator: John Day, M.D. |
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Washington University School of Medicine
Saint Louis, MO
Principal Investigator: Anne Connolly
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Duke University Medical Center
Durham, NC
Principal Investigator- Stephanie Burns-Wechsler, M.D.
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Columbia University Medical School
New York City, NY
Principal Investigator: Petra Kaufmann, M.D. |
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Cincinnati Children's Hospital
Cincinnati, OH
Principal Investigator: Brenda Wong, M.D.
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Shriners Hospital for Children
Portland, OR
Principal Investigator: Barry Russman, M.D.
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Children's Hospital of Philadelphia
Philadelphia, PA
Principal Investigator: Richard Finkel, M.D.
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Southwestern University
Dallas, TX
Principal Investigator: Susan Iannacone, M.D.
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University of Utah
Salt Lake City, UT
Principal Investigator: Kevin Flanigan, M.D. |
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