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 Ataluren for Genetic
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 PTC299 Oncology

The ataluren (PTC124™) Phase 2b trial in nonsense mutation Duchenne and Becker muscular dystrophy involves 37 sites on four continents, as shown on the map below. As you click on each region, you will be able to see names and locations of specific sites. The trial is a multi-center, randomized, double-blind, placebo-controlled study to determine whether ataluren can improve walking, activity, muscle function, and strength and whether the drug can safely be given for a long period of time.

Australia

 

         
  Royal Children's Hospital
Parkville, Victoria

Principal Investigator: Monique Ryan, M.D.
 

Institute For Neuromuscular
Research, The Children's Hospital at Westmead

Westmead, NSW

Principal Investigator: Kristi Jones, M.D.

Belgium

 

         
 

University Hospital KU Leuven
Leuvan, Belgium

Principal Investigator: Nathalie Goemans, M.D.

    

Canada

 

         
 

Alberta Children's Hospital
Calgary, Alberta

Principal Investigator: Jean Mah, M.D.

  London Health Sciences Center
London, Ontario

Principal Investigator: Craig Campbell, M.D.

 

British Columbia Children's Hospital
Vancouver, British Columbia

Principal Investigator: Katherine Selby, M.D.

    
 
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France

 

         
  Service de Neuropediatrie, hôpital La Timone
Marseille, France

Principal Investigator: Brigitte Chabrol, M.D.

 

Neuromuscular center of Nantes
Nantes, France

Principal Investigator: Yann Pereon, M.D.

 

Groupe Hospitalier La Pitie-Salpetriere
Paris, France

Principal Investigator: Thomas Voit, M.D.

    
 

Germany

 

         
  University Clinic for Children, University of Essen
Essen, Germany

Principal Investigator: Ulrike Schara, M.D.
  University Hospital
Freiburg, Germany

Principal Investigator: Jan Kirschner, M.D.

Israel

 

         
  Hadassah Medical Center, Hebrew University Hospital
Jerusalem, Israel

Principal Investigator: Yoram Nevo, M.D.
    
 
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Italy

 

         
  Ospedale Maggiore Policlinico in Milan
Milan, Italy

Principal Investigator: Pr. Giacomo Comi, M.D.
 

Ospedale Pediatrico Bambino Gesu
Rome, Italy

Principal Investigator: Enrico Bertini, M.D.

 

U.O. Complessa di Neuropsichiatria Infantile
Rome, Italy

Principal Investigator: Eugenio Mercuri, M.D.

 

    
 

Spain

 

         
 

Hospital Sant Joan de déu
Barcelona, Spain

Principal Investigator: Jaume Colomer, M.D.

  Hospital Universitari La Fe
Valencia, Spain

Sweden

 

         
 

Queen Silvia Children's Hospital
Goteburg, Sweden

Principal Investigator: Mar Tulinius, M.D.

 

Astrid Lindgren Pediatric Hospital
Stockholm, Sweden

Principal Investigator: Thomas Sejersen, M.D.

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United Kingdom

 

         
 

Imperial College London, Hammersmith Hospital
London, UK

Principal Investigator: Francesco Muntoni, M.D.

 

Univ of Newcastle, Institute of Human Genetics
Newcastle, UK

Principal Investigator: Katharine Bushby, M.D.

 

Robert Jones and Agnes Hunt Orthopaedic NHS Trust
Shropshire, UK

Principal Investigator:Ros Quinlivan, M.D.

    
 

USA

 

         
 

University of California-Davis
Sacramento, CA

Principal Investigator: Craig McDonald, M.D.

 

The Children's Hospital
Aurora, CO

Principal Investigator: Susan Apkon, M.D.

 

Child Neurology Center of Pensacola
Pensacola, FL

Principal Investigator: Ben Renfroe, M.D.

 

University of Iowa Healthcare
Iowa City, IA


Principal Investigator: Kathy Mathews, M.D.

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  University of Kansas Medical Centre
Kansas City, KS

Principal Investigator:Richard Barohn, M.D.
 

Children's Hospital of Boston/Harvard Medical School
Boston, MA

Principal Investigator: Basil Darras, M.D.

  University of Minnesota
Minneapolis, MN

Principal Investigator: John Day, M.D.
 

Washington University School of Medicine
Saint Louis, MO

Principal Investigator: Anne Connolly

 

Duke University Medical Center
Durham, NC

Principal Investigator- Stephanie Burns-Wechsler, M.D.

  Columbia University Medical School
New York City, NY

Principal Investigator: Petra Kaufmann, M.D.
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Cincinnati Children's Hospital
Cincinnati, OH

Principal Investigator: Brenda Wong, M.D.  

 

Shriners Hospital for Children
Portland, OR

Principal Investigator: Barry Russman, M.D.

 

Children's Hospital of Philadelphia
Philadelphia, PA

Principal Investigator: Richard Finkel, M.D.

 

Southwestern University
Dallas, TX

Principal Investigator: Susan Iannacone, M.D.

 

University of Utah
Salt Lake City, UT

Principal Investigator: Kevin Flanigan, M.D.

 

 



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