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The PTC124 Phase 2b trial in Duchenne muscular dystrophy and Becker muscular dystrophy will involve more than 35 sites on 4 continents. Use the map below to locate the study site closest to you. As you click on each region, you will be able to see names and locations of specific sites. As each study site opens (indicated by a green dot), information will be added so that you can contact the site of your choice directly.



Australia

 

  Royal Children's Hospital
Parkville, Victoria


Contact: Daniella Villano
+61-3-9345-4633
daniella.villano@rch.org.au

Principal Investigator: Monique Ryan, M.D.
 

Institute For Neuromuscular
Research, The Children's Hospital
at Westmead

Westmead, NSW

Belgium

 

 

University Hospital KU Leuven
Leuvan, Belgium

Contact: Greet Leemputten

+32 16 34 38 45

greet.vanleemputten@uz.kuleuven.ac.be

Prinicpal Investigator: Nathalie Goemans, M.D.

    

Canada

 

  Alberta Children's Hospital
Calgary, Alberta
  London Health Sciences Center
London, Ontario

Contact: Ashrafunissa Janmohammad
519-685-8207
ashrafu.nissa@lhsc.on.ca

Principal Investigator: Craig Campbell, M.D.

  British Columbia Children's Hospital
Vancouver, British Columbia
    
 
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France

 

  Service de Neuropediatrie, hôpital La Timone
Marseille, France
 

Neuromuscular center of Nantes
Nantes, France

Contact: Raphaelle Chasserieau
Phone: +33-24-008-3617
Raphaelle.Chasserieau@chu-nantes.fr

Principal Investigator: Yann Pereon, M.D.

  Groupe Hospitalier La Pitie-Salpetriere
Paris, France
    
 

Germany

 

  University Clinic for Children, University of Essen
Essen, Germany

Contact: Barbel Leiendecker
+49-201-723-2508
baerbel.leiendecker@uk-essen.de

Principal Investigator: Ulrike Schara, M.D.
  University Hospital
Freiburg, Germany

Contact: Ursula Wein
+49-761-270-7711
ursula.wein@uniklinik-freiburg.de

Principal Investigator: Jan Kirschner, M.D.

Israel

 

  Hadassah Medical Center, Hebrew University Hospital
Jerusalem, Israel
    
 
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Italy

 

  Ospedale Maggiore Policlinico in Milan
Milan, Italy
  Ospedale Pediatrico Bambino Gesu
Rome, Italy
  U.O. Complessa di Neuropsichiatria Infantile
Rome, Italy
    
 

Spain

 

  Hospital Sant Joan de déu
Barcelona, Spain
  Hospital Universitari La Fe
Valencia, Spain

Sweden

 

 

Queen Silvia Children's Hospital
Goteburg, Sweden

Contact: Ulrica Sterky
+46-31-343-8207
ulrika.sterky@vgregion.se

Principal Investigator: Mar Tulinius, M.D.

  Astrid Lindgren Pediatric Hospital
Stockholm, Sweden
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United Kingdom

 

  Imperial College London, Hammersmith Hospital
London, UK
  Univ of Newcastle, Institute of Human Genetics
New Castle, UK
  Robert Jones and Agnes Hunt Orthopaedic NHS Trust
Shropshire, UK
    
 

USA

 

  University of California-Davis
Sacramento, CA
  The Children's Hospital
Aurora, CO
 

Child Neurology Center of Pensacola
Pensacola, FL

Contact: Holley Moseley

850-484-6060

holley.moseley@childneurologycenter.com

Principal Investigator: Ben Renfroe, M.D.

 

University of Iowa Healthcare
Iowa City, IA


Contact: Carrie Stephan
319-356-2673

carrie-stephan@uiowa.edu

Prinicpal Investigator: Kathy Mathews, M.D.

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  University of Kansas Medical Centre
Kansas City, KS

Contact: Victoria Watts
913-588-5479
vwatts@kumc.edu

Principal Investigator:Richard Barohn, M.D.
  Children's Hospital of Boston/Harvard Medical School
Boston, MA
  University of Minnesota
Minneapolis, MN
 

Washington University School of Medicine
Saint Louis, MO

Contact: Betsy Malkus

314-362-1624

malkusb@neuro.wustl.edu

Principal Investigator: Anne Connolly

 

Duke University Medical Center
Durham, NC

Contact: JoAnne Mackey
919-684-2036
macke003@mc.duke.edu

Principal Investigator- Stephanie Burns-Wechsler, M.D.

  Columbia University Medical School
New York City, NY

Contact: Jackie Montes
212-342-5767
JMontes@neuro.columbia.edu

Principal Investigator: Petra Kaufmann, M.D.
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University of Rochester
Rochester, NY

Contact: Alexis Smirnow
585-275-4715
alexis_smirnow@urmc.rochester.edu

Principal Investigator: Emma Ciafaloni, M.D.

  Cincinnati Children's Hospital
Cincinnati, OH

Contact: Paula Morehart
513-636-8967
Paula.Morehart@cchmc.org

Principal Investigator: Brenda Wong, M.D.  
  Shriners Hospital for Children
Portland, OR
 

Children's Hospital of Philadelphia
Philadelphia, PA


Contact: Lindsay Dorsey
267-426-7623
dorsey@email.chop.edu

Principal Investigator: Richard Finkel, M.D.

  Southwestern University
Dallas, TX

Contact: Medrith Green
214-456-8072
medrith.greene@childrens.com

Principal Investigator: Susan Iannacone, M.D.
 

University of Utah
Salt Lake City, UT

Contact: Brianna McGerty
801-585-1299 bmcgerty@genetics.utah.edu

Principal Investigator: Kevin Flanigan, M.D.



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