A FEW IMPORTANT RESOURCES FOR PATIENTS AND FAMILIES:

Action Duchenne
www.actionduchenne.org

Association Francaise Contre Les Myopathies (AFM)
www.afm-france.org

Canadian Organization for Rare Disorders
www.raredisorders.ca

Cystic Fibrosis Foundation (CFF)
www.cff.org

Duchenne Parent Project Onlus
www.parentproject.org

European Organization for Rare Disorders (EURORDIS)
www.eurordis.org

FDA Clinical Trials Website
www.clinicaltrials.gov

Gene Tests: NIH-Sponsored Website
www.genetests.org

Muscular Dystrophy Association
www.mdausa.org

National Organization for Rare Disorders (NORD)
www.rarediseases.org

Parent Project Muscular Dystrophy (PPMD)
www.parentprojectmd.org

TREAT-NMD Neuromuscular Network
(Translational Research in Europe for the Assessment and
Treatment of Neuromuscular Disease)
www.treat-nmd.eu

Vaincre La Mucoviscidose
www.vaincrelamuco.org

* Please note that external web site links provided in this document are outside of PTC Therapeutics' control, and we assume no responsibility for the information they may contain. This document is provided for educational purposes only and is not intended to replace the medical advice of a physician or other qualified health care provider.