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 Genetic Disorders: PTC124
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A FEW IMPORTANT RESOURCES FOR PATIENTS AND FAMILIES:

Association Francaise Contre Les Myopathies (AFM)
www.afm-france.org

Cystic Fibrosis Foundation (CFF)
www.cff.org

European Organization for Rare Disorders (EURORDIS)
www.eurordis.org

FDA Clinical Trials Website
www.clinicaltrials.gov

Gene Tests: NIH-Sponsored Website

www.geneclinics.org

Muscular Dystrophy Association
www.mdausa.org

National Organization for Rare Disorders (NORD)
www.rarediseases.org

Parent Project Muscular Dystrophy (PPMD)
www.parentprojectmd.org

Treat NMD Neuromuscular Network (Translational Research in Europe for the Assessment and Treatment of Neutomuscular Disease)

www.treat-nmd.eu

Vaincre La Mucoviscidose
www.vaincrelamuco.org

 

*Please note that external web site links provided in this document are outside of PTC's Therapeutics' control, and we assumes no responsibility for the information they may contain.

 

 

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